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Gene Editing Therapy Articles & Analysis: This-Year
2 articles found
Poor fixation and tracking behaviors in infants and young children can arise from a wide range of underlying causes. Imaging modalities such as fundus photography, fundus autofluorescence, fluorescein angiography, and optical coherence tomography are available but typically require anesthesia. The saccadic vector optokinetic perimeter (SVOP), with its built-in eye-tracking, was designed to ...
Rare diseases collectively affect hundreds of millions of people worldwide, yet many individual conditions remain difficult to diagnose and treat due to their low prevalence and complex biological mechanisms. In recent decades, therapeutic enzymes have emerged as an important class of biologic drugs that address the underlying causes of several rare genetic disorders. By replacing or ...