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Gain Transplanter Equipment & Supplies
3 equipment items found
by:Gain Therapeutics, Inc. based inBethesda, MARYLAND (USA)
Very limited and investigational symptomatic treatment options include substrate reduction therapy, enzyme replacement therapy, bone marrow transplantation, stem cell transplantation and gene therapy to address non-CNS symptoms. Gain is developing allosteric regulators that are designed to decrease toxic substrate accumulation in organs and tissues of patients ...
by:Gain Therapeutics, Inc. based inBethesda, MARYLAND (USA)
Very limited and investigational symptomatic treatment options include substrate reduction therapy, enzyme replacement therapy, bone marrow transplantation, stem cell transplantation and gene therapy to address non-CNS symptoms. Gain is developing allosteric regulators that are designed to decrease toxic substrate accumulation in organs and tissues of patients ...
by:Gain Therapeutics, Inc. based inBethesda, MARYLAND (USA)
There is currently no cure for these patients; however, enzyme replacement therapy and hematopoietic stem cell transplant are used to manage the non-CNS symptoms. Gain is developing allosteric regulators to increase IDUA activity and decrease toxic sugar accumulation in the CNS of patients with MPS 1 to potentially become the first treatment for the disease’s neuronopathic ...