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Wakix - Pitolisant Tablets for Rare Metabolic and Endocrine Diseases - Medical / Health Care
The endocrine and metabolic system includes endocrine glands and endocrine tissues, which regulate human function by secreting hormones. Endocrine diseases are rare and often very difficult to diagnose and treat. Among the 121 rare diseases included on China’s national list of rare diseases in 2018, more than 20 are endocrine/metabolic-related rare diseases.
People living with a rare disease are at the center of everything we do at Citrine.
We focus on building access to treatments for the 20 million rare disease patients in China who have very few options available to them. We aim to deliver innovative therapies and to make a positive impact on the lives of patients.We focus on rare neurological, metabolic/endocrine, renal/liver and pediatric oncology diseases.