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Gene Replacement Therapy Suppliers In North America
60 companies found
based inSouth San Francisco, CALIFORNIA (USA)
Neurona Therapeutics is driven by rigorous scientific discovery and focused on developing breakthrough treatments for neurological disorders. Neurona Therapeutics is a privately-held, clinical-stage biotherapeutics company focused on discovering and ...
Neurona’s lead product candidate, NRTX-1001, comprises human MGE-type inhibitory GABAergic interneurons derived from pluripotent stem cells. NRTX-1001’s first indication is for the treatment of drug-resistant focal epilepsy, which is a ...
based inSanta Barbara, CALIFORNIA (USA)
Owl Biomedical, Inc. was founded in 2011 to expand the use of its exclusive cell sorting MEMS technology for cell therapy, cancer diagnostics and basic research. Operating in Santa Barbara, California, Owl Biomedical was purchased in 2013 by ...
based inBoston, MASSACHUSETTS (USA)
Neoclease is at the forefront of advancing gene editing technologies with a mission to transform healthcare by curing genetic diseases rather than just treating them. Utilizing a bespoke approach, the company develops tailored nucleases designed to ...
based inHamburg, GERMANY
Revvity Gene Delivery (formerly SIRION Biotech) supports your cell and gene therapy development process ̶ offering solutions for early R&D all the way to clinical applications, with easy transfer of processes and assays into GMP production. ...
At Revvity, we work with you to expedite the development of gene therapy vectors. ...
based inAllendale, NEW JERSEY (USA)
We are a leading global contract development and manufacturing organization (CDMO) dedicated to the advancement and manufacturing of gene and cell therapy products. Minaris Regenerative Medicine is a leading global contract development and ...
At Minaris Regenerative Medicine, we are committed to bringing together and further developing highly talented, skilled, and dedicated experts with varied backgrounds applicable to gene and cell therapy manufacturing and development. Having this ...
based inSomerset, NEW JERSEY (USA)
As the global leader in enabling pharma, biotech, and consumer health partners to optimize product development, launch, and full life-cycle supply for patients around the world, we conduct all our business responsibly and with integrity. Our ...
Drug product development can be a daunting and expensive process. Biotech companies face many hurdles along the way, including the development and optimization of a scalable, commercially viable formulation while ensuring safety and efficacy of the ...
based inMadison, WISCONSIN (USA)
Mirus continued the development of a wide range of non-viral delivery technologies using proteins, polymers, and lipids in conjunction with novel chemistries that provided unique nucleic acid delivery capabilities. Our work at Mirus Bio began with a ...
based inMumbai, INDIA
Krishgen BioSystems (Krishgen) is privately-owned biotech firm with academic linkages to provide tools to scientists. With the strong background in immunology, we believe in the delivering quality kits, reagents and consumables. Certified and ...
Adeno-Associated Virus (AAV) is a nonpathogenic virus that is widely used as vector in gene therapy. KRISHGEN currently provides full range of adeno-associated virus (AAV) assay kits that specifically recognize intact virus capsids as well as ...
based in, NEW JERSEY (USA)
Tevogen Bio is driven by a team of distinguished scientists and experienced biopharmaceutical leaders who have developed and commercialized multiple franchises. In collaboration with key strategic partners, the company moved its lead product from ...
based inSan Carlos, CALIFORNIA (USA)
CellFE is a venture-backed company with a mission to make advanced therapies accessible to all by transforming the way gene therapies are manufactured. The company uses a microfluidics-based cell engineering platform that can be adapted universally ...
based inPhiladelphia, PENNSYLVANIA (USA)
A clinical-stage biotechnology company focused on the discovery and development of engineered T cell therapies for B cell-mediated autoimmune diseases Cabaletta Bio seeks to employ its specifically targeted CAAR (Chimeric AutoAntibody Receptor) T ...
based inNew York, NEW YORK (USA)
Altucell, Inc. is a cellular engineering and biotech company backed by sound research and science focused on fulfilling a large 'unmet need' in cell, molecular and regenerative therapy for treatment of Diabetes and other autoimmune and ...
based inSouth San Francisco, CALIFORNIA (USA)
Senti Bio was founded to create a new generation of smarter medicines that outmaneuver complex diseases using novel and unprecedented approaches. Senti Bio designs and optimizes gene circuits, which are created from novel and proprietary ...
Senti Bio has established, and continues to scale, a powerful Design-Build-Test-Learn development engine to generate our therapeutic gene circuits. Unique to Senti Bio’s approach is the speed, quantity and quality of the multiple types of gene ...
based inBrisbane, CALIFORNIA (USA)
Mammoth Biosciences is harnessing the diversity of nature to power the next generation of CRISPR products. Through its discovery of novel CRISPR systems, the company is enabling the full potential of its platform to read and write the code of life. ...
Discovering novel CRISPR systems: We are addressing the current challenges of CRISPR-Cas systems and expanding the scope of use by applying our proprietary discovery platform to identify novel Cas ...
based inLimerick, PENNSYLVANIA (USA)
Rockland Immunochemicals, Inc. offers a robust catalog of antibodies to suit any project. No matter the context—basic research to disease therapy, phosphorylated to methylated, and beyond—Rockland embraces the challenge to design, produce, validate, ...
From virus production and titering to pre-GMP research and assay development, the experienced team at Rockland provides custom virology services to advance the development of protein therapeutics, cell and gene therapies, vaccines, and ...
based inCollege Station, TEXAS (USA)
Matica Biotechnology is a cell and gene therapy CDMO that is bringing together integrated GMP manufacturing platforms and innovative solutions resulting in speed to clinic without sacrificing quality. Our investments in advanced, single-use ...
At Matica Biotechnology’s 25,000-square-foot GMP facility in College Station, Texas, we offer fully integrated solutions for cell and gene therapies, vaccines, oncolytic vectors and other biotherapeutic ...
based inHollister, CALIFORNIA (USA)
Teknova has been innovating how custom critical reagents are manufactured for the life sciences industry since 1996. Founded by Genentech scientist Ted Davis in Half Moon Bay, California, Teknova was established with the goal of helping scientists ...
based inGaithersburg, MASSACHUSETTS (USA)
In November 2023, Selecta Biosciences Inc. (NASDAQ: SELB) merged with Cartesian Therapeutics to create a publicly traded company pioneering RNA cell therapy to treat autoimmune disease. The combined company will focus on advancing Cartesian’s wholly ...
Selecta Biosciences’ immune tolerance platform, ImmTOR, is designed to give rise to antigen-specific immunity, mitigating unwanted immune ...
based inBall Ground, GEORGIA (US) (USA)
The MVE range of cryogenic freezers and aluminum dewars have been engineered for ultimate reliability and maximizing hold times at the ultra-low temperatures vital to the preservation of critical human and animal tissues and vaccines. We supply a ...
based inWinston-Salem, NORTH CAROLINA (USA)
Charter Medical, LLC has nearly 35 years of experience developing and providing specialty single-use products to the cell therapy, blood transfusion, biotechnology, and pharmaceutical markets. Our 16,000 square feet of cleanroom space located in ...
Bring your cell therapy processes together seamlessly with an extensive range of standard and customized fluid transfer solutions. Charter Medical’s fluid transfer sets are optimal for sterile transfer of cell and fluid material between unit ...
