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Genetic Disorder Suppliers & Manufacturers
40 companies found
based inEatonton, GEORGIA (US) (USA)
Since 1979 Aalto Scientific has been a leader in the manufacture of OEM/Private label quality controls and calibrators, purified human proteins, and bulk human and animal sera to the in vitro diagnostic (IVD) manufacturing community. With over 40 ...
Homocysteine Control is a stable liquid product intended to simulate human patient samples for the purpose of monitoring the precision of laboratory testing procedures for ...
based inGangnam-gu, SOUTH KOREA
MitoImmune Therapeutics Inc. is a drug discovery and development biotech company that harnesses the power of mitochondria and its proprietary technology targeting mitochondria as the source for developing new potential breakthrough therapeutics. Our ...
based inAlameda, CALIFORNIA (USA)
Scribe is focused on the engineering, delivery, and development of next-generation CRISPR molecules to rewrite and repair the underlying cause of genetic ...
based inMalvern, PENNSYLVANIA (USA)
Ocugen Inc. (NASDAQ: OCGN) is a biopharmaceutical company focused on discovering, developing, and commercializing gene therapies to cure blindness diseases and developing a vaccine to fight COVID-19. Our breakthrough modifier gene therapy platform ...
OCU400 (AAV-NR2E3) is a novel gene therapy product candidate with the potential to be broadly effective in restoring retinal integrity and function across a range of genetically diverse inherited retinal diseases (“IRDs”). It consists of ...
based inMerelbeke, BELGIUM
Ziphius Vaccines is named after the rare dolphin Ziphius cavirostris. This dolphin is most known for undertaking the deepest and longest dives recorded. Ziphius' mission is to reduce the global impact of infectious diseases on global health care by ...
Self-amplifying RNA (saRNA) or replicon RNA has the advantage of having self-replicating features, as the saRNA molecule encodes a viral RNA replicase in addition to the sequence of the protein(s) of interest. Upon cytoplasmic delivery of the saRNA ...
based inRostock, GERMANY
Since 2006, CENTOGENE has helped physicians diagnose thousands of rare disease patients around the world. A quick and accurate diagnosis can end an odyssey of medical tests and visits to multiple medical specialists. It also helps physicians better ...
Genetic testing is a type of medical test that identifies changes in genes, inherited from our parents, which we then typically pass on to our children. “Mistakes” in our genes (called “pathogenic variants”) can manifest the ...
based inMunich, GERMANY
The technological progress made in biomedical research has radically changed the view to new treatment strategies. Modern genetic technologies can deliver disease-relevant targets but are insufficient to refill the empty drug discovery pipeline. We ...
based inOxford, UNITED KINGDOM
Evox Therapeutics is a privately held, Oxford-based biotechnology company focused on improving the natural delivery capabilities of exosomes, and developing an entirely new class of therapeutics. Backed by leading venture capital groups and ...
Argininosuccinic aciduria (ASA) is a rare genetic disorder characterized by a deficiency or lack of the enzyme argininosuccinate lyase (ASL). ...
based inGermantown, MARYLAND (USA)
Cell and gene therapies (CGTs) use modified cells or cellular matter to treat, prevent or cure serious health issues like cancer, genetic disorders, immunodeficiencies, rare diseases, and more. CGTs have shown potential to replace damaged cells with ...
based inMontreal, QUEBEC (CANADA)
As a specialty therapeutics, clinical-stage biotech company, Inversago Pharma develops new generations of peripherally-acting cannabinoid-1 receptor (CB1) inverse agonists for the treatment of diabetic kidney disease, type 1 and type 2 diabetes, ...
based in, MASSACHUSETTS (USA)
MtoZ Biolabs is an integrate contract research organization (CRO) providing advanced proteomics, metabolomics, bioinformatics, and biopharmaceutical analysis services to researchers in biochemistry, biotechnology, and biopharmaceutical fields. The ...
based inAbbiategrasso, ITALY
Since 1987, Clonit has been focused in developing, manufacturing and distributing of innovative and reliable in Vitro Diagnostic Equipment and Reagents for Molecular Diagnostics. A deep expertise in Molecular Biology mixed to our strong culture of ...
based inPleasanton, CALIFORNIA (USA)
29 years designing high affinity antibodies and immunoassays. Proudly serving the brightest minds in scientific research. Your experts in offering state-of-the-art ELISA kits, antibodies, custom reagents and analytical services in immunology, ...
Gene therapy is a method of delivering therapeutic genes to cells or tissues using modified viruses or other technologies in order to address genetic disorders at their source. The understanding of how the ...
based inClayton, GEORGIA (US) (USA)
GenSol was founded in 2008 to address the growing need for canine genetic screening and the everyday application of increasingly complex biological assays using state-of-the-art technology. Accurate and affordable genetic testing for a multitude of ...
Laryngeal paralysis (LP) is a genetic disorder that results in breathing difficulties which can be made worse by physical activity and may lead to suffocation in severe cases. The condition may require surgery to ...
based inPune, INDIA
RASA Life Science Informatics, a highly-regarded organization, has gained recognition from Biotech Consortium India Limited (BCIL) and is based in Pune, India. They not only provide research and development services but also offer a comprehensive ...
How Our Gene Expression Analysis Services Can Help You ? Genes encode proteins and proteins dictate cell function. Therefore, the thousands of genes expressed in a particular cell determine what that cell can do. Moreover, each step in the flow of ...
based inVancouver, BRITISH COLUMBIA (CANADA)
InMed Pharmaceuticals is a global leader in the pharmaceutical research, development and manufacturing of rare cannabinoids and cannabinoid analogs, including clinical and preclinical programs targeting the treatment of diseases with high unmet ...
based inZirakpur, INDIA
Opdenas Lifesciences is one of the best ophthalmic and ENT based PCD Pharma Franchise Companies in India, having developed a niche in eye, ear, and nasal drops. We carry a large selection of DCGI-approved ophthalmic and ENT products. The portfolio ...
based inSan Rafael, CALIFORNIA (USA)
Established in 1997, BioMarin is a world leader in developing and commercializing first- or best-in-class therapies for rare genetic diseases. We take pride in going where the science leads us, pioneering breakthrough treatments for debilitating and ...
In alignment with our commitment to scientific innovation and areas of unmet medical need, we may provide product and funding support for independent research in rare diseases and genetic ...
based inSultanbeyli – Istanbul, TURKEY
Anatolia Geneworks is a biotechnology company operating in accordance with ISO 9001, ISO 13485 and 98/79/EC Total Quality Systems. The main activities of Anatolia Diagnostics and Biotechnology Inc. are to develop and manufacture Real-Time Polymerase ...
Familial Mediterranean fever (FMF) is an autosomal recessive genetic disorder, which occurs commonly in Mediterranean countries causing symptoms such as recurrent acute fever, abdominal pain, joint pain etc. FMF ...
based inJerusalem, ISRAEL
BrainQ Technologies developing breakthrough precision neurology therapies using Brain Computer Interface technology. BrainQ’s goal is to develop therapies that target damaged neuronal networks and facilitate neurorecovery. We are developing a ...