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Gene Replacement Therapy Suppliers Serving Paraguay
62 companies found
based inCranbury, NEW JERSEY (USA)
Advancing an integrated pipeline of genetic therapies that correct the root cause of complex and rare life-threatening childhood disorders. Our mission is to develop first-in-class and best-in-class, curative gene therapies for patients with ...
Danon Disease (DD) is a rare genetic disorder that is characterized by severe and primarily hypertrophic cardiomyopathy. Skeletal muscle weakness and mild cognitive impairment are also common. The causative mutation has been identified in the gene ...
based inCambridge, MASSACHUSETTS (USA)
Myeloid Therapeutics is a leader in the development of mRNA-based immunotherapies, focusing on harnessing and enhancing the natural capabilities of myeloid cells to combat cancer. The company's cutting-edge in vivo engineering platform is designed ...
based inColumbus, OHIO (USA)
Andelyn Biosciences is a biopharmaceutical CDMO Pioneering Solutions That Turn Hope into Reality™. With 20+ years of experience manufacturing viral vectors, Andelyn’s scientific expertise for development and characterization has led to GMP material ...
Andelyn Biosciences provides clients with a broad range of viral vector manufacturing platforms and solutions, including AAV and Lentiviral adherent and suspension systems along with plasmid manufacturing. We support our clients throughout every ...
based inDublin, IRELAND
Our mission is to help clients accelerate the development of drugs and devices that save lives and improve quality of life. We offer a full range of consulting, clinical development and commercialisation services from a global network of offices in ...
Accelerating study start-up and delivering results with custom strategies and logistics solutions. ICON helps navigate the Cell and Gene Therapy journey by overcoming challenges and mitigating risks. Almost every cell and gene therapy clinical trial ...
based inNew York, NEW YORK (USA)
Altucell, Inc. is a cellular engineering and biotech company backed by sound research and science focused on fulfilling a large 'unmet need' in cell, molecular and regenerative therapy for treatment of Diabetes and other autoimmune and ...
based inHamburg, GERMANY
Revvity Gene Delivery (formerly SIRION Biotech) supports your cell and gene therapy development process ̶ offering solutions for early R&D all the way to clinical applications, with easy transfer of processes and assays into GMP production. ...
At Revvity, we work with you to expedite the development of gene therapy vectors. ...
based inTurku, FINLAND
Biovian is a Bio-CDMO that provides services to biotech companies developing innovative gene therapies or biopharmaceuticals. Our goal is to turn ideas into products by taking client projects from the laboratory bench to the clinic. To do so we ...
Adenoviruses are attractive tools for gene therapy, including immuno-oncology, because of their well-defined biology and characteristics including the possibility for large gene inserts. Biovian has proven expertise in adenovirus vector process ...
based inMadison, WISCONSIN (USA)
Mirus continued the development of a wide range of non-viral delivery technologies using proteins, polymers, and lipids in conjunction with novel chemistries that provided unique nucleic acid delivery capabilities. Our work at Mirus Bio began with a ...
based inPleasanton, CALIFORNIA (USA)
We’re all about helping biologics and gene therapy researchers break free from tools that just don’t cut it. Unleashing problem-tackling products that make a huge difference in the real science they do every day. That’s our mantra, our promise and ...
Stunner is the only system that pulls together UV/Vis concentration, Dynamic Light Scattering (DLS) and Static Light Scattering (SLS) data from the same 2 μL sample. Dig in to your AAV to get the total capsid titer and empty/full ratio, or rack ...
based inOttawa, ONTARIO (CANADA)
Virica was founded in 2018 based on a decade of research in the laboratory of Dr. Jean-Simon Diallo at the Ottawa Hospital Research Institute. Dr. Diallo was investigating novel oncolytic viral therapies (OVTs) and recognized the need for VSEs to ...
Viral Medicines are the Way of the Future. Gene therapies and vaccines save and protect human life. The COVID-19 pandemic highlights the criticality of vaccine development today and into the future. The pandemic also highlights the challenges drug ...
based inAustin, TEXAS (USA)
OriGen Biomedical, Inc. is a leading producer of cryopreservation, cell culture, and respiratory products. OriGen’s focus is to produce a range of products to support the treatment of respiratory distress, cancer, genetic conditions, and other ...
based inSan Diego, CALIFORNIA (USA)
Resilience is your biomanufacturing innovation partner, leading the pursuit of novel medicines by revolutionizing how they’re made, funded and scaled. The technology of manufacturing complex medicines, like cell and gene therapies, hasn’t kept pace ...
based inPlanegg, GERMANY
TQ Therapeutics GmbH is pioneering a novel approach to cell and gene therapy with its TQx platform, which transforms the production of cellular therapies into a rapid, automated process that occurs at the patient's side. This method leverages ...
TQx is developing a modular target cell-specific modification platform including relevant technology components for the generation of gene modified cell therapy ...
based inGangnam-gu, SOUTH KOREA
Kangstem Biotech promotes a step-by-step business strategy to optimize its success rate of new global medicine development. Kangstem Biotech will create a world where people can enjoy a healthy and happy life by developing stem cell therapeutic ...
based inMumbai, INDIA
Krishgen BioSystems (Krishgen) is privately-owned biotech firm with academic linkages to provide tools to scientists. With the strong background in immunology, we believe in the delivering quality kits, reagents and consumables. Certified and ...
Adeno-Associated Virus (AAV) is a nonpathogenic virus that is widely used as vector in gene therapy. KRISHGEN currently provides full range of adeno-associated virus (AAV) assay kits that specifically recognize intact virus capsids as well as ...
based inBarcelona, SPAIN
SpliceBio is a cutting-edge genetic medicine company specializing in Protein Splicing as a novel modality for gene therapy. Rooted in advancements from the Muir Lab at Princeton University, the company leverages over two decades of pioneering ...
SpliceBio specializes in addressing the challenges of gene therapy by leveraging engineered split inteins. Traditional adeno-associated virus (AAV) vectors are limited by size, restricting their ability to package only small genes, thus leaving many ...
based inStratford-upon-Avon, UNITED KINGDOM
Our team of world-class scientists and biotechnology leadership is devoted to discovering breakthrough medicines that change the standard of medical care for patients. Sir Martin Evans, Nobel Laureate, and Ajan Reginald, former Global Head of ...
based inVillejuif, FRANCE
Stilla Technologies is the multiplex digital PCR company transforming complex genomic data into actionable insights across a wide range of research and clinical applications including cancer and liquid biopsy studies, cell and gene therapies, ...
based inSouth San Francisco, CALIFORNIA (USA)
Senti Bio was founded to create a new generation of smarter medicines that outmaneuver complex diseases using novel and unprecedented approaches. Senti Bio designs and optimizes gene circuits, which are created from novel and proprietary ...
Senti Bio has established, and continues to scale, a powerful Design-Build-Test-Learn development engine to generate our therapeutic gene circuits. Unique to Senti Bio’s approach is the speed, quantity and quality of the multiple types of gene ...
based inCollege Station, TEXAS (USA)
Matica Biotechnology is a cell and gene therapy CDMO that is bringing together integrated GMP manufacturing platforms and innovative solutions resulting in speed to clinic without sacrificing quality. Our investments in advanced, single-use ...
At Matica Biotechnology’s 25,000-square-foot GMP facility in College Station, Texas, we offer fully integrated solutions for cell and gene therapies, vaccines, oncolytic vectors and other biotherapeutic ...