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Vimizim Bladder Control Equipment & Supplies In Micronesia

1 equipment items found
Available In MicronesiaNear Micronesia

Vimizim - Model MPS IVA - Elosulfase Alfa for Morquio A Syndrome

Vimizim - Model MPS IVA - Elosulfase Alfa for Morquio A Syndrome

Manufactured by:BioMarin   based inSan Rafael, CALIFORNIA (USA)
Vimizim (elosulfase alfa) is the first approved enzyme replacement therapy designed to address the underlying cause of Morquio A syndrome, or mucopolysaccharidosis IVA (MPS IVA) — a deficiency in the enzyme N-acetylgalactosamine-6 sulfatase (GALNS). VIMIZIM works at a cellular level to help with deficient enzyme ...
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