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Gain Morquio B Bone Marrow Equipment & Supplies
1 equipment items found
by:Gain Therapeutics, Inc. based inBethesda, MARYLAND (USA)
Very limited and investigational symptomatic treatment options include substrate reduction therapy, enzyme replacement therapy, bone marrow transplantation, stem cell transplantation and gene therapy to address non-CNS symptoms. Gain is developing allosteric regulators that are designed to decrease toxic substrate accumulation in organs and tissues of patients ...