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Galafold Clinical Linked Data Equipment & Supplies In Africa
1 equipment items found
Manufactured by:Amicus Therapeutics, Inc. based inPhiladelphia, PENNSYLVANIA (USA)
Galafold® is indicated for the treatment of adults with a confirmed diagnosis of Fabry disease and an amenable galactosidase alpha gene (GLA) variant based on in vitro assay data. This indication is approved under accelerated approval based on reduction in kidney interstitial capillary cell globotriaosylceramide (KIC GL-3) substrate. Continued approval for this indication may be contingent ...
