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Gain Demyelination Equipment & Supplies
1 equipment items found
by:Gain Therapeutics, Inc. based inBethesda, MARYLAND (USA)
These mutations cause GALC misfolding and dysfunction, which leads to the toxic buildup up fats in the central nervous system (CNS) and ultimately leads to the demyelination and death of neurons. There is no cure for this disease and most patients will die before the age of two. Gain is developing allosteric regulators to restore GALC function and potentially limit neuronal cell ...