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Hereditary Disease Equipment Supplied In Europe
2 equipment items found
by:Astraveus based inParis, FRANCE
Hematopoietic stem cells (HSCs) are mothers to all blood cells including erythrocytes and lymphocytes. We develop high quality genetically edited HSCs to cure an undisclosed hereditary blood disease. This development will be translatable: genetically edited HSCs can be used to treat multiple genetic diseases, including hemoglobinopathies and ...
by:Gain Therapeutics, Inc. based inBethesda, MARYLAND (USA)
GM1 Gangliosidosis is a hereditary, progressive disease mostly impacting neurons in the brain and spinal cord, caused by mutations in GLB1, the gene that encodes the beta-galactosidase (GLB) enzyme. These mutations result in the misfolding and subsequent dysfunction of GLB, which leads to the toxic substrate accumulation of GM1 ganglioside in organs and tissues. ...