Genetic Predisposition For Celiac Disease Equipment Supplied In Spain
1 equipment items found
Manufactured by:SpliceBio based inBarcelona, SPAIN
SpliceBio is developing several gene therapy programs aimed at treating genetic diseases by exploiting our proprietary Protein Splicing platform. Our lead program is in Stargardt disease, the most common inherited retinal disorder caused by mutations in a single gene, ABCA4, which at 6.8 kb is too large for single AAV ...
