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Lentiviral Vector Equipment Supplied In Usa New Jersey
5 equipment items found
Manufactured by:Rocket Pharmaceuticals, Inc. based inCranbury, NEW JERSEY (USA)
The process involves collection and isolation of a patient’s hematopoietic stem cells (HSCs), insertion of the corrected gene into the HSCs via a lentiviral vector outside the body, and the infusion of modified HSCs back into the patient. The goal is to enable sufficient quantities of a healthy, disease-modifying therapeutic protein to be manufactured by ...
Manufactured by:Rocket Pharmaceuticals, Inc. based inCranbury, NEW JERSEY (USA)
The process involves collection and isolation of a patient’s hematopoietic stem cells (HSCs), insertion of the corrected gene into the HSCs via a lentiviral vector outside the body, and the infusion of modified HSCs back into the patient. The goal is to enable sufficient quantities of a healthy, disease-modifying therapeutic protein to be manufactured by ...
Manufactured by:Rocket Pharmaceuticals, Inc. based inCranbury, NEW JERSEY (USA)
FA is a rare, genetic disorder affecting DNA repair. Approximately two-thirds of FA cases are caused by genetic defects in the FANCA gene, which results in the FA subtype known as FA Complementation Group A (FA-A). FA patients may develop bone marrow failure (very low blood counts), cancers of the blood or other ...
Manufactured by:Rocket Pharmaceuticals, Inc. based inCranbury, NEW JERSEY (USA)
PKD is a rare, genetic blood disorder. PKD is caused by a defect in the PKLR gene which is responsible for energy production in red blood cells (RBCs). RBCs carry oxygen to the rest of the body. When the PKLR gene has a defect, RBCs are limited in their ability to produce energy and remain intact. As a result, patients with PKD frequently have anemia, chronic fatigue, yellowing of the skin and ...
Manufactured by:Rocket Pharmaceuticals, Inc. based inCranbury, NEW JERSEY (USA)
LAD-I is a rare genetic disorder affecting the immune system and is caused by a defect in the ITGB2 gene, leading to a deficiency in CD18. Due to this deficiency, white blood cells (primarily neutrophils) are unable to leave the bloodstream to go to the site of infection. As a result, patients with severe LAD-I can develop life-threatening infections which they are unable to fight. Without a ...