Rocket Pharmaceuticals, Inc.

Advancing an integrated pipeline of genetic therapies that correct the root cause of complex and rare life-threatening childhood disorders. Our mission is to develop first-in-class and best-in-class, curative gene therapies for patients with devastating diseases. Our vision is “Seeking Gene Therapy Cures”. Our company values of Trust, Be Generous, Be Curious and Elevate are at the heart of all that we do. Our strategic approach to gene therapy has positioned us to launch a sustainable multi-platform pipeline of treatments that directly target the genetic mutation in the affected cells for rare, life-threatening childhood disorders, including Fanconi Anemia (FA), Leukocyte Adhesion Deficiency-I (LAD-I), Danon Disease, Pyruvate Kinase Deficiency (PKD) and multiple undisclosed diseases.