Human Disease Biology Articles & Analysis
8 news found
About SeqOne Genomics SeqOne Genomics offers high-performance genomic analysis solutions for healthcare providers treating patients suffering from cancer, rare and hereditary diseases as well as pharmaceutical companies developing new therapies. ...
High blood glucose can lead to diabetic ketoacidosis and over time, to complications such as kidney disease/failure, eye disease (including vision loss), heart disease, stroke, nerve damage and even death. ...
“It’s an honor to join Vertex, a company focused on serial innovation with an industry-leading track record of discovering, developing and commercializing transformative medicines to treat serious diseases. It is particularly exciting to join at such a pivotal time, when the company is in the process of transforming the treatment of multiple serious ...
Cell and genetic therapies are two rapidly emerging therapeutic modalities with the potential to treat the underlying cause — and even cure — several of the serious diseases Vertex is working on including sickle cell disease, beta thalassemia, type 1 diabetes and Duchenne muscular dystrophy. ...
” “I want patients to feel there is somebody in their corner because this disease affects every facet of their lives,” said Sharl Azar, M.D., Medical Director for the Mass General Comprehensive Sickle Cell Disease Treatment Center. ...
High blood glucose can lead to diabetic ketoacidosis and over time, to complications such as kidney disease/failure, eye disease (including vision loss), heart disease, stroke, nerve damage and even death. ...
About Cystic Fibrosis Cystic fibrosis (CF) is a rare, life-shortening genetic disease affecting more than 83,000 people globally. CF is a progressive, multi-organ disease that affects the lungs, liver, pancreas, GI tract, sinuses, sweat glands and reproductive tract. ...
If positive, the interim analysis may serve as the basis for Vertex to seek accelerated approval of VX-147 in the U.S. for patients with AMKD. About APOL1-Mediated Kidney Disease APOL1-mediated kidney disease is a form of chronic kidney disease caused by mutations in the APOL1 gene. ...