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Rare Disease Equipment & Supplies
43 equipment items found
by:Healx Ltd. based inCambridge, UNITED KINGDOM
The world’s most efficient AI platform for rare disease drug discovery, supporting our teams and partners in our mission to advance new treatments towards the ...
Manufactured by:InvivoSciences, Inc. (IVS) based inMadison, WISCONSIN (USA)
InvivoSciences (IVS) combines its human micro tissue technology and phenotypic assay platform with the systems biology approach to achieve rare disease modeling for its drug discovery. Our strip tissues are perfect for modeling muscle and connective tissue in micro-well plates. Since many rare diseases affect heart muscle and ...
by:Oligomerix, Inc. based inWhite Plains, NEW YORK (USA)
There exist numerous rare diseases that tau dysfunction is associated with known as tauopathies. While Alzheimer’s is the largest tauopathy, other tauopathies are rare diseases that present accelerated regulatory pathways and significant near-term commercial opportunities. These rare ...
Manufactured by:Bausch Health Companies Inc. based inLaval, QUEBEC (CANADA)
Our diversified portfolio of well-established specialty pharmaceuticals targets several therapeutic areas, including epilepsy, migraines, depression, chronic pain, and rare diseases such as Huntington's disease. ...
by:Alexion Pharmaceuticals, Inc. based inBoston, MASSACHUSETTS (USA)
People with rare diseases often wait years to receive a proper diagnosis and many never receive one at all. RARE ANSWERS™ is a system of innovative and sustainable tools designed to help shorten the diagnostic journey and time to initiating treatment of children with a rare disease. Developed in ...
by:Healx Ltd. based inCambridge, UNITED KINGDOM
Our Rare Treatment Accelerator helps academic, patient, and industry groups advance their rare disease drug redevelopment projects. By combining our team, expertise and financial resources with your research and insights, we can get treatments to patients ...
by:Pure Biologics SA based inWroclaw, POLAND
Myasthenia gravis (MG) is an autoimmune condition classified as a rare disease. Accordingly, myasthenic patients lack effective treatment options, as this rare disease is not a primary interest of the pharmaceutical industry. However, considerable social and institutional support exists for the development of new therapies to ...
by:Pure Biologics SA based inWroclaw, POLAND
Neuromyelitis optica (NMO) is an neurological autoimmune condition classified as a rare disease. Because of this classification, NMO lacks effective treatment options, since it is not of primary interest to the pharmaceutical industry. However, considerable social and institutional support exists for developing new therapies for such rare ...
Manufactured by:Lipella Pharmaceuticals Inc. based inPittsburgh, PENNSYLVANIA (USA)
The potential uses of this registry about radiation cystitis and hemorrhagic cystitis (and cancer survivorship post-radiotherapy) include: improving the scientific understanding of radiation cystitis, discovering trends and common needs of registry participants, describing the aggregate personal characteristics of radiation cystitis patients within the registry, documenting registry patient ...
Manufactured by:MedChemExpress LLC (MCE) based inMonmouth Junction, NEW JERSEY (USA)
Mifamurtide is a specific ligand for NOD2 and acts as an insulin sensitizer. Mifamurtide has potential for use in rare disease and osteosarcoma ...
Manufactured by:MedChemExpress LLC (MCE) based inMonmouth Junction, NEW JERSEY (USA)
Mifamurtide sodium is a specific ligand for NOD2 and acts as an insulin sensitizer. Mifamurtide sodium has potential for use in rare disease and osteosarcoma ...
Manufactured by:Twist Bioscience based inSouth San Francisco, CALIFORNIA (USA)
Twist Exome 2.0 is designed to detect rare and inherited diseases, as well as germline cancers. This panel’s high uniformity and low off-target rate deliver best-in-class sequencing efficiency, enabling quality data to be collected with less sequencing. With superior coverage of major genetic databases (RefSeq, CCDS, GenCode, Clinvar, ACMG73 and more) and ...
by:Palvella Therapeutics. based inWayne, PENNSYLVANIA (USA)
QTORIN™ rapamycin 3.9% is a novel targeted topical therapy being studied for Microcystic Lymphatic Malformations (Micro LM). Palvella is enrolling a phase 2 clinical study for people with Micro ...
Manufactured by:Tonix Pharmaceuticals Holding Corp. based inChatham, NEW JERSEY (USA)
TNX-2900, Tonix’s proprietary potentiated intranasal oxytocin is in the pre-Investigational New Drug (IND) stage as a candidate for the treatment of Prader-Willi syndrome (PWS) and non-organic failure to thrive disease. TNX-2900 has been granted Orphan Drug Designation (ODD) in the US by the FDA for the treatment of ...
Manufactured by:Evox Therapeutics Limited based inOxford, UNITED KINGDOM
Niemann-Pick C disease (NPC) is a lysosomal storage disorder which affects the brain and multiple other ...
Manufactured by:Catalent, Inc based inSomerset, NEW JERSEY (USA)
Gene therapy holds the promise of treating the unmet needs of patients who suffer from a rare genetic disease. An estimated 4,000 medical conditions are a result of gene disorders with no previous targeted treatments. Gene therapy offers new options away from the conventional symptomatic approach to disease treatment as well as provides hope for ...
Manufactured by:CENTOGENE N.V. based inRostock, GERMANY
The CentoPharma platform provides intelligent access to our comprehensive data repository that combines phenotype, genotype and biochemistry information with epidemiological data and clinical information from a global cohort originating from more than 120 countries. Dynamic search criteria enable the targeted compilation of individual customized cohorts based on desired geographical region, ...
Distributed by:Salehiyah Establishment based inRiyadh, SAUDI ARABIA
Explore our diversified portfolio of pharmaceuticals, as we deliver the right medication to the right patient at the right time, covering some of the most critical needs of patients in the Kingdom. ...
Manufactured by:Suvoda based inConshohocken, PENNSYLVANIA (USA)
Our advanced patient randomization and trial supply management system. Your clinical trial command and control ...
Manufactured by:Diaceutics PLC based inBelfast, UNITED KINGDOM
What is DXRX Signal? DXRX Signal delivers an actionable alert of a testing behavior that allows you to engage a physician whilst they are making treatment decisions, therefore maximizing the effectiveness of your brand sales and ...