Rare Disease Services In Belgium
2 services found
by:Genome Biologics based inFrankfurt am Main, GERMANY
Kearns-Sayre Syndrome (KSS) is a mitochondrial disease, with Rare Disease designation (7,400 – 22,000 patients in Europe), caused primarily by large-scale mitochondrial DNA deletions. Cardiac dysfunction is the principal clinical manifestation and primary cause of death. There are no current treatment options available that go beyond ...
by:CuraVac Europe S.A. based inRixensart, BELGIUM
Myasthenia Gravis (MG) is a rare, but not exceptional, autoimmune disease that is diagnosed (Prevalence) in one in seven thousand (1.33/10,000) to one per five thousand (2/10,000) of the population. It is characterized by muscular fatigue leading to extreme weakness. ...