Lysosomal Storage Disease Articles & Analysis
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The concept is straightforward: supplying a functional enzyme helps correct the metabolic imbalance that causes disease symptoms. Therapeutic Enzymes in Lysosomal Storage Disorders One of the most successful applications of therapeutic enzymes is in the treatment of lysosomal storage disorders (LSDs). These ...
One example is lysosomal storage disease. This group of diseases is defined as lysosomal dysfunction, which results in delayed growth, deafness, or dementia. ...