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Lysosomal Storage Disease Suppliers & Manufacturers
3 companies found
based inNew York City, NEW YORK (USA)
Lauren Sciences is a privately-held New York biotechnology company focused on developing its V-Smart platform to create a robust pipeline of V-Smart therapeutics consisting of central nervous system (CNS)-active drugs that normally do not cross the ...
based inNaarden, NETHERLANDS
Azafaros has leveraged on decades of discovery by professors Hans Aerts, Hermen Overkleeft, and Stan van Boeckel at Leiden University and the Academic Medical Center in the Netherlands. Expanding on their research and led by highly experienced ...
Their lead compound, nizubaglustat, leverages unique dual-mode action, making it a promising candidate for modifying diseases irrespective of patient genotypes. Notably effective against conditions such as GM1 and GM2 gangliosidoses ...
based inNewburypor, MASSACHUSETTS (USA)
At EnClear Therapies, our goal is to improve and extend the lives of patients with a wide variety of CNS disease through precision dosing. We are building an Integrated Neurotechnology Business using our CSF Health Platform to create a pipeline of ...