Muscular Disease Articles & Analysis
4 articles found
The balance of inflammatory and anti-inflammatory signals produced by SMECs is crucial, as dysregulation can lead to chronic inflammation, often associated with conditions such as muscular dystrophy and other muscle-wasting diseases. Beyond their roles in blood flow regulation and inflammation, SMECs contribute to metabolic functions within skeletal muscle. ...
This therapeutic gene, once inside the cell, generates a functional protein to correct or counter the effects of the disease-causing genetic mutation, providing a basis for curing several genetic diseases. ...
Gene Therapy Viral Vector Development for Rare Diseases Development of Adenoviral Vectors Develop adenoviral vectors that produce milder immune responses to deliver larger DNA packages with less risk, accelerating the development of effective gene therapies for rare diseases. ...
Cardiovascular safety liabilities caused 52.3 % of 44 marketed data from 1980 to 2011, and cardiovascular disease remains the leading cause of death globally, yet only 8.7% of cardiovascular drugs successfully pass clinical trials. ...