Muscular Disease Articles & Analysis
8 news found
Viral vectors can be used for the treatment of various diseases such as: muscular, metabolic, hematologic, ophthalmologic, and infectious diseases as well as different types of cancer. ...
ByNuvonis
The Muscular Dystrophy Association is pleased to announce the award of an MDA Venture Philanthropy (MVP) grant totaling $233,200 to Scottsdale, ...
BynVector
Every year, the month of August is nationally recognized as Spinal Muscular Atrophy (SMA) Awareness Month. This month-long awareness campaign serves as an important time to demonstrate support and help promote awareness for this rare disease affecting lives across the world. ...
Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) and Mammoth Biosciences, a biotech company building the next generation of CRISPR products to cure and detect disease, today announced a new partnership to develop in vivo gene-editing therapies for two genetic diseases using Mammoth’s next-generation CRISPR systems. ...
“The ability to tune gene-editing activity to a specific level is an important innovation that has the potential to address several serious diseases.” “At Obsidian, we’re using our cytoDRiVE technology to pioneer a new generation of engineered cell and gene therapies for patients with serious diseases,” said Paul Wotton, Chief ...
UNITY improves clinical specificity for cystic fibrosis carrier screening UNITY is the only prenatal screen that tests cell-free fetal DNA for cystic fibrosis, spinal muscular atrophy (SMA), sickle cell disease, and alpha and beta thalassemia using just one tube of blood from the mother. ...
A non-invasive prenatal test for Alpha Thalassemia Hb Barts and Hb Constant Spring UNITY is the only prenatal screen that tests cell-free fetal DNA for cystic fibrosis, spinal muscular atrophy (SMA), sickle cell disease, and alpha and beta thalassemia using just one tube of blood from the mother. Alpha Thalassemia is a frequent and severe recessive genetic ...
CATEGORY “IDEAS/BUSINESS PROJECTS” Miramoon Pharma: New molecules aimed at treating diseases based on muscular dystrophy. Multiverse Computing: Quantum computing solutions and advanced artificial intelligence applied to finance and economics. Onena Medicines: Biotechnology company focused on the development of first-class medicines to treat ...