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Gene Replacement Therapy Suppliers Near American Samoa
90 companies found
based inMilpitas, CALIFORNIA (USA)
ASC Therapeutics is a fully incorporated biopharmaceutical company focusing on the development of curative therapeutic products that are enabled by our proprietary gene editing platform, TARGATT and other gene editing technologies developed after 12 ...
We are developing gene and cell-based therapies. Gene therapy is addition, alteration or removal of genes within cells and biological tissues to treat diseases. A correcting genetic agent can be delivered directly to the blood stream in vivo, or to ...
based inMalvern, PENNSYLVANIA (USA)
Ocugen Inc. (NASDAQ: OCGN) is a biopharmaceutical company focused on discovering, developing, and commercializing gene therapies to cure blindness diseases and developing a vaccine to fight COVID-19. Our breakthrough modifier gene therapy platform ...
OCU400 (AAV-NR2E3) is a novel gene therapy product candidate with the potential to be broadly effective in restoring retinal integrity and function across a range of genetically diverse inherited retinal diseases (“IRDs”). It consists of ...
based inBarcelona, SPAIN
SpliceBio is a cutting-edge genetic medicine company specializing in Protein Splicing as a novel modality for gene therapy. Rooted in advancements from the Muir Lab at Princeton University, the company leverages over two decades of pioneering ...
SpliceBio specializes in addressing the challenges of gene therapy by leveraging engineered split inteins. Traditional adeno-associated virus (AAV) vectors are limited by size, restricting their ability to package only small genes, thus leaving many ...
based inBoston, MASSACHUSETTS (USA)
Neoclease is at the forefront of advancing gene editing technologies with a mission to transform healthcare by curing genetic diseases rather than just treating them. Utilizing a bespoke approach, the company develops tailored nucleases designed to ...
based inCarpi, ITALY
IGEA S.p.A. is a biomedical company and a world leader in biophysical therapies. Our activities focus on the study of interactions between biological systems and physical stimuli used for therapeutic purposes. IGEA therapies can be applied in ...
Incorporates a commercial syringe housing, guiding the injection to the centre of the electroporation volume. Easy control of needle insertion depth, as needles remain in the guide. Option to inject to different depths. Mechanical retraction of the ...
based inFoxborough, MASSACHUSETTS (USA)
Suono Bio is a biotechnology company harnessing our proprietary delivery platform to transform treatment of intractable diseases. Suono Bio is a on a mission to harness its proprietary therapeutic platform to transform treatment of ...
based inCambridge, MASSACHUSETTS (USA)
Obsidian Therapeutics is using its proprietary cytoDRiVE platform to harness the power of proteins to engineer precision medicines. Our lead internal programs are focused on engineering TIL therapies that are more effective and safer for patients ...
Engineered with membrane-bound IL15, Eliminates toxic IL2 regimen, increasing patient accessibility to TIL therapy, Drives improved persistence, IL15 expression controlled by acetazolamide (ACZ), via cytoDRiVE® ...
based inSan Diego, CALIFORNIA (USA)
Resilience is your biomanufacturing innovation partner, leading the pursuit of novel medicines by revolutionizing how they’re made, funded and scaled. The technology of manufacturing complex medicines, like cell and gene therapies, hasn’t kept pace ...
based inPhiladelphia, PENNSYLVANIA (USA)
Chimeron Bio is building a portfolio of self-amplifying RNA therapeutics and vaccines to bring more effective gene therapies and personalized medicines to patients. We are developing a compelling portfolio of innovative and personalized saRNA-based ...
based inTokyo, JAPAN
We create plug-and-play bio-manufacturing solutions using our unique cell culture platform technology, CellFiber™, to enable higher yields and product quality and ensure stability, predictability, reproducibility, and scalability of cells for cell ...
based inAllendale, NEW JERSEY (USA)
We are a leading global contract development and manufacturing organization (CDMO) dedicated to the advancement and manufacturing of gene and cell therapy products. Minaris Regenerative Medicine is a leading global contract development and ...
At Minaris Regenerative Medicine, we are committed to bringing together and further developing highly talented, skilled, and dedicated experts with varied backgrounds applicable to gene and cell therapy manufacturing and development. Having this ...
based inLaramie, WYOMING (USA)
GlycoBac has developed a sensitive assay for infectious Sf-rhabdovirus particles using our proprietary Sf-RVN cell line. GlycoBac has partnered with MilliporeSigma to facilitate the distribution of our Sf-RVN cell line for commercial vaccine and ...
based inJerusalem, ISRAEL
Betalin Therapeutics licensed the novel Engineered Micro Pancreas (EMP) technology developed at The Hebrew University of Jerusalem, Israel, in an exclusive worldwide agreement in 2015. The Hebrew University continues to partner with Betalin ...
based inCranbury, NEW JERSEY (USA)
Advancing an integrated pipeline of genetic therapies that correct the root cause of complex and rare life-threatening childhood disorders. Our mission is to develop first-in-class and best-in-class, curative gene therapies for patients with ...
Danon Disease (DD) is a rare genetic disorder that is characterized by severe and primarily hypertrophic cardiomyopathy. Skeletal muscle weakness and mild cognitive impairment are also common. The causative mutation has been identified in the gene ...
based inStratford-upon-Avon, UNITED KINGDOM
Our team of world-class scientists and biotechnology leadership is devoted to discovering breakthrough medicines that change the standard of medical care for patients. Sir Martin Evans, Nobel Laureate, and Ajan Reginald, former Global Head of ...
based inNEW YORK (USA)
Our company is a globally operating service provider and one of the world leaders in the development and delivery of advanced drug therapies for rare diseases. We not only provide global customers with a wide range of services for rare disease ...
based in, DISTRICT OF COLUMBIA (USA)
Lovelace Biomedical is very much focused on gene therapy for genetic diseases testing in human clinical trials. Our ultimate aim is to give best gene therapy medicine. Lovelace Biomedical is a contract research organization that focuses on ...
Lovelace Biomedical is very much focused on gene therapy for genetic diseases testing in human clinical trials. Our ultimate aim is to give best gene therapy medicine. http://www.lovelacebiomedical.org/specialty-expertise/gene-therapy/ ...
based inRochester, MINNESOTA (USA)
Cytotheryx, Inc. is a preclinical cell therapy company focused on the development of a readily available, consistent and high-quality source of primary human hepatocytes (liver cells) and the use of those cells for research and clinical ...
At Cytotheryx, we understand that life-saving discovery in liver disease research and medicine requires a multi-faceted approach. The key to enabling this innovation is a reliable foundation. We understand this need and the opportunity to support ...
based inSan Carlos, CALIFORNIA (USA)
CellFE is a venture-backed company with a mission to make advanced therapies accessible to all by transforming the way gene therapies are manufactured. The company uses a microfluidics-based cell engineering platform that can be adapted universally ...
based inMerelbeke, BELGIUM
Ziphius Vaccines is named after the rare dolphin Ziphius cavirostris. This dolphin is most known for undertaking the deepest and longest dives recorded. Ziphius' mission is to reduce the global impact of infectious diseases on global health care by ...
Proteins are large biological macromolecules that are essential parts of organisms and participate in virtually every process within cells. Proteins are created through the process of gene expression, in which genetic information from DNA is ...